Ivacaftor for Cystic Fibrosis
Molecular visualization in a 2-page spread
Cystic Fibrosis is a serious genetic disease that causes deficits in fluid transport of epithelial cells. It's characterized by the sticky mucus in lung and multiple organ dysfunction. In 2012, Ivacaftor was approved by U.S. Food and Drug Administration (FDA). It is the very first drug to treat the cause of cystic fibrosis and it was granted the first Breakthrough Therapy designation to cystic fibrosis by FDA. This 2-page spread takes a deep dive into the disease pathogenesis and visualize how the therapy works in a bimolecular scale.
Faculty advisor
Derek Ng
Medium/Software
VMD, 3D Protein Imager, Autodesk Maya, and Adobe Illustrator
Final presentation format
A two page spread in a scientific magazine
Primary audience
The general public with a science background
Work Process
Reference
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PBD ID: 6MSM, 5UAK, and 6O2P
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Zhang, Z., Liu, F., & Chen, J. (2018). Molecular structure of the ATP-bound, phosphorylated human CFTR. Proceedings of the National Academy of Sciences, 115(50), 12757–12762. https://doi.org/10.1073/pnas.1815287115
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Liu, F., Zhang, Z., Csanády, L., Gadsby, D. C., & Chen, J. (2017). Molecular Structure of the Human CFTR Ion Channel. Cell, 169(1), 85–95.e8. https://doi.org/10.1016/j.cell.2017.02.024
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Liu, F., Zhang, Z., Levit, A., Levring, J., Touhara, K. K., Shoichet, B. K., & Chen, J. (2019). Structural identification of a hotspot on CFTR for potentiation. Science, 364(6446), 1184–1188. https://doi.org/10.1126/science.aaw7611
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Bompadre, S. G., Sohma, Y., Li, M., & Hwang, T. C. (2007). G551D and G1349D, Two CF-associated Mutations in the Signature Sequences of CFTR, Exhibit Distinct Gating Defects. Journal of General Physiology, 129(4), 285–298. https://doi.org/10.1085/jgp.200609667
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National Center for Biotechnology Information (2021). PubChem Compound Summary for CID 16220172, Ivacaftor. Retrieved July 16, 2021 from https://pubchem.ncbi.nlm.nih.gov/compound/Ivacaftor.
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Cystic Fibrosis | NHLBI, NIH. (2021, May 12). National Heart, Lung and Blood Institute. https://www.nhlbi.nih.gov/health-topics/cystic-fibrosis